Development of a Gene Therapy Delivery System for the Treatment of Hereditary Retinopathy-Intraocular Injection and Eye Drops Formulations( I )

Project: A - Government Institutionb - Ministry of Science and Technology

Project Details

Description

本計畫主要在利用新穎的奈米載體技術用於眼睛穿透,發展解決遺傳性視網膜變性疾病的療法,其中的手段包含基因治療與藥物傳遞療法。同時,試量產並企圖與業界結合,以朝向臨床前試驗為計畫未來的最終目標。
StatusActive
Effective start/end date8/1/227/31/23

Keywords

  • inherited retinal diseases
  • mesoporous silica nanoparticles
  • homology-independent targeted integration
  • retinoschisin-1
  • 3D retinal organoid